Minicircle DNA-based Gene Therapy Coupled With Immune Modulation Permits Long-term Expression of α-L-Iduronidase in Mice With Mucopolysaccharidosis Type I
Osborn, Mark J, McElmurry, Ron T, Lees, Christopher J, DeFeo, Anthony P, Chen, Zhi-Ying, Kay, Mark A, Naldini, Luigi, Freeman, Gordon, Tolar, Jakub, Blazar, Bruce RТом:
19
Мова:
english
Журнал:
Molecular Therapy
DOI:
10.1038/mt.2010.249
Date:
March, 2011
Файл:
PDF, 468 KB
english, 2011