Long-term restoration of thymidine phosphorylase function and nucleoside homeostasis using hematopoietic gene therapy in a murine model of MNGIE
Torres-Torronteras, Javier, Cabrera-Pérez, Raquel, Barba, Ignasi, Costa, Carme, de Luna, Noemí, Andreu, Antoni L, Barquinero, Jordi, Hirano, Michio, Cámara, Yolanda, Marti, RamonМова:
english
Журнал:
Human Gene Therapy
DOI:
10.1089/hum.2015.160
Date:
March, 2016
Файл:
PDF, 2.04 MB
english, 2016