Long-term stability in randomized and non-randomized patients in the phase 3 randomized, double-blind EDGE trial of once- versus twice-daily dosing of eliglustat in patients with Gaucher disease type 1
Charrow, Joel, Fraga, Cristina, Gu, Xuefan, Ida, Hiroyuki, Longo, Nicola, Lukina, Elena, Nonino, Alexandre, Gaemers, Sebastiaan J.M., Jouvin, Marie-Helene, Li, Jing, Wu, Yaoshi, Xue, Yong, Judith PeteТом:
123
Мова:
english
Журнал:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2017.12.054
Date:
February, 2018
Файл:
PDF, 51 KB
english, 2018