Genetically Corrected iPSC-Derived Neural Stem Cell Grafts Deliver Enzyme Replacement to Affect CNS Disease in Sanfilippo B Mice
Clarke, Don, Pearse, Yewande, Kan, Shih-hsin, Le, Steven Q., Sanghez, Valentina, Cooper, Jonathan D., Dickson, Patricia I., Iacovino, MichelinaТом:
10
Мова:
english
Журнал:
Molecular Therapy - Methods & Clinical Development
DOI:
10.1016/j.omtm.2018.06.005
Date:
September, 2018
Файл:
PDF, 3.96 MB
english, 2018