[BMJ Publishing Group Ltd EHDN 2018 Plenary Meeting, Vienna, Austria, Programme and Abstracts - ()] Experimental therapeutics â preclinical - I05â Sustained mutant huntingtin lowering in the brain and cerebrospinal fluid of huntington disease minipigs mediated by AAV5-MIHTT gene therapy
Valls, Astrid, Brouwers, Cynthia, Pintauro, Roberta, Snapper, Jolanda, Bohuslavova, Bozena, Sogorb-Gonzalez, Marina, Fodale, Valentina, Bresciani, Alberto, Ellederova, Zdenka, Blits, Bas, Motlik, Jan,Рік:
2018
DOI:
10.1136/jnnp-2018-ehdn.241
Файл:
PDF, 68 KB
2018